Review and meta-analysis of real-world efficacy with data in Type II and Type III patients presented by Prof. Mercuri and Dr. Coratti
“Now we see the patients frequently and now we recognize that SMA during adulthood is a progressive disease.”
“Now we see the patients frequently and now we recognize that SMA during adulthood is a progressive disease.” 1 min
“If we want to pick up that the patient moves better one finger, that is not something we see in the scales - but patients do report it.” 1 min
“The main treatment goal in the Adult patients is a stabilisation of the disease course… of motor function… of the ability to breathe and to speak language” 1 min
Biogen-173724-HK-09/22